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Mirum Pharmaceuticals
Registrace 19. 08. 2019
Mirum is creating transformative medicine for children with rare cholestatic liver disease.
Mirum Pharmaceuticals is dedicated to creating life-changing therapies for patients with liver diseases. We are advancing our lead product candidate for Alagille syndrome (ALGS) and progressive familial intrahepatic cholestasis (PFIC) - conditions with a profound and devastating impact on quality of life for young patients and their families.
Mirum Pharmaceuticals is dedicated to creating life-changing therapies for patients with liver diseases. We are advancing our lead product candidate for Alagille syndrome (ALGS) and progressive familial intrahepatic cholestasis (PFIC) - conditions with a profound and devastating impact on quality of life for young patients and their families.
Video
Mirum ALGS Series: Caregiver Perspective
zhlédnutí 249Před rokem
For more information about ALGS and support options, visit www.mirumpharma.com and www.alagille.org.
Through Their Eyes: Life With Cholestatic Pruritus in Alagille Syndrome
zhlédnutí 3,1KPřed rokem
Restless, irritable, scratching. For children with Alagille syndrome, this is their reality. Watch one family’s struggle to cope with unrelenting itch, known as cholestatic pruritus, the most burdensome symptom of Alagille syndrome. See the different ways it can impact and disrupt their daily lives. Based on a true story. #Alagillesyndrome #cholestaticpruritus If you are a patient or caregiver ...
The ALGS Caregiver Experience
zhlédnutí 102Před rokem
Caregivers of children with rare diseases are superheroes. Hear more about the ALGS caregiver experience and how caregivers often carry the burden of these symptoms along with their loved ones. For more information about ALGS and support options, visit www.mirumpharma.com and www.alagille.org.
Mirum PFIC Series: Cedar
zhlédnutí 418Před rokem
Mirum is committed to creating life-changing therapies for patients like Cedar. For more information on Mirum, visit mirumpharma.com. Progressive Familial Intrahepatic Cholestasis (PFIC) is a rare genetic condition that causes progressive liver disease, often leading to liver failure and requiring a liver transplant. In patients with PFIC, liver cells are less able to eliminate bile, leading to...
Introducing, Itch✓™-A Powerful Tool to Help You Log Symptoms
zhlédnutí 201Před 2 lety
Itch✓-Check it. Chart it. Discuss it.™ Itch✓ is a simple, yet detailed symptom journal designed to help you and your doctor make sense of itch severity, personal statistics, and more
Disease State Overview of Intrahepatic Cholestasis of Pregnancy (ICP)
zhlédnutí 978Před 3 lety
Learn more about the rare cholestatic liver disease, intrahepatic cholestasis of pregnancy, also known as ICP. Mirum Chief Medical Officer Dr. Ed Tucker sat down with Drs. Catherine Williamson of King's College and Katherine Kohari of Yale School of Medicine to discuss ICP, how and why it occurs, a profile of the patients, an overview of clinical studies that have been conducted to date, and th...
Mirum ALGS Series: Jocelyn
zhlédnutí 625Před 3 lety
Mirum is committed to creating life-changing therapies for patients like Jocelyn. For more info about clinical studies and treatment availability, please contact us at info@mirumpharma.com, or visit algseap.com for updates and to sign up for notifications about the Expanded Access Program for children with ALGS. ALGS is a rare genetic disorder in which bile ducts are abnormally narrow, malforme...