Prophylaxis in Hemophilia: Past, Present and Future

Discover the latest breakthroughs in hemophilia treatment with pediatric experts as they explore cutting-edge therapies that could change lives for those with the condition. These breakthroughs are discussed in the context of the Joint Outcome Study and Joint Outcome Continuation Study, which re-defined the standard of care in hemophilia.
In this video, Drs. Beth Warren and Marilyn Manco-Johnson discuss the importance of early prophylaxis in reducing osteochondral damage for those with hemophilia and the challenges of providing consistent clotting factor replacement therapy. They also examine promising new products in development, such as longer-acting factor proteins and emicizumab, an engineered antibody that offers a more convenient treatment option. Also, learn about the first hemophilia gene therapy treatment recently approved by the FDA in November 2022.
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[@alexandar5253]

Is there a possibility that hemophilia will be cured in 10-15 years with gene therapy? And will it be free in some county's? My son has the hemophilia A and we live in Croatia,the profilaxis is free in our country,what about gene therapy? Please answer, thanks in advance