First Patient Receives Gene Therapy for Rare Liver Disorder

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  • čas přidán 25. 07. 2018
  • An investigational gene therapy for glycogen storage disease (GSD) was administered to a patient for the first time ever on July 24. Dr. David Weinstein and his team administered the one-time, 30-minute infusion at UConn John Dempsey Hospital. The gene therapy gives real hope to patients who suffer from the potentially deadly GSD - a rare childhood genetic disorder impacting the liver’s storage and release of sugar. Watch the video to meet Jerrod and see him receive this groundbreaking therapy.

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