for now its to prevent few to zero bleeds. But its my hope that they can infuse kids at a young age so they can have a somewhat normal child hood. Its still in clinical trial phase hoping to be FDA approved soon as a treatment
@Sakib Farazi there’s not cure for hemophilia the gene therapy is just so that your body can start thinking you have the factor that’s missing so that ur able to clot my levels before gene therapy was 0.01% now it higher than that
@@myhemophilialife7345 iam hemophilia moderate and i think gene therapy will cure all genetics disease also hemophilia cure too but difficult for severe and cause also inhibitors so you are not same bro, i know there are no cure yet but gene therapy coming soon and effective hobe and promising its can Change life on the way iam mean cure permanent and solution, maybe your have problem other,I think U don’t have experience on gene therapy maybe Don't mind i just said my opinion
I would love to hear about an update!
Will definitely post one
shots fired!!!! lol so the goal of gene therapy is to prevent the disorder from being passed on? Was the treatment successful?
for now its to prevent few to zero bleeds. But its my hope that they can infuse kids at a young age so they can have a somewhat normal child hood. Its still in clinical trial phase hoping to be FDA approved soon as a treatment
@@myhemophilialife7345 was it effective?
@@MeloIsland yes it has been working for me. A lot more I could say but not on this platform due to legal reasons
@@myhemophilialife7345 as long as it works
Its possible to cure hemophilia and solution ever? And how much your factor level right now and was before gene therapy? Please tell me bro
@Sakib Farazi there’s not cure for hemophilia the gene therapy is just so that your body can start thinking you have the factor that’s missing so that ur able to clot my levels before gene therapy was 0.01% now it higher than that
@@myhemophilialife7345 how much factor level now yor after gene therapy?
@@myhemophilialife7345 iam hemophilia moderate and i think gene therapy will cure all genetics disease also hemophilia cure too but difficult for severe and cause also inhibitors so you are not same bro, i know there are no cure yet but gene therapy coming soon and effective hobe and promising its can Change life on the way iam mean cure permanent and solution, maybe your have problem other,I think U don’t have experience on gene therapy maybe Don't mind i just said my opinion